We strike at the core of serious diseases to change people’s lives. Bringing together the brightest minds, investing in science and taking smart risks, we go all in. For the lives we have changed and for those who are still waiting, we will never stop fighting until we discover cures. We have research and development sites and commercial offices around the world, all dedicated to bringing the next transformative treatments to people with serious diseases. Our headquarters are in Boston and London.

We believe in the promise and potential of science to have a transformative impact for people living with serious diseases. It’s how we create value for patients, families and society as a whole. It’s why we dedicate the vast majority of resources toward innovation, from building teams of top talent to creating a robust toolkit of technologies — all of our efforts are aimed at treating serious diseases. We invest in science so people can live better lives. 

When we decide to work on a disease, we investigate it from every angle. For example, our sickle cell disease and beta thalassemia programs include multiple approaches. We've developed a gene-editing treatment that is currently approved in some countries for certain eligible people living with sickle cell disease or transfusion-dependent beta thalassemia.

At the same time, we continue to advance our research to discover and develop new conditioning regimens with the aim of improving the stem cell transplant process, and explore oral small molecule treatment options.

We’re investing in cell and genetic therapies to build an industry-leading portfolio of technologies, teams and manufacturing capabilities. We're committed to pushing the scientific envelope by leveraging emerging therapeutic modalities that have the potential to have a transformative impact for patients who are waiting.  

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